Mirum Pharmaceuticals to Participate in Upcoming Investor Conferences

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FOSTER CITY, Calif.--(BUSINESS WIRE)--Aug 27, 2025--

Mirum Pharmaceuticals, Inc. (Nasdaq: MIRM), a biopharmaceutical company focused on the identification, acquisition, development and commercialization of novel therapies for debilitating rare and orphan diseases, today announced that it will participate in the following upcoming investor conferences:

• Citi Biopharma Back-to-School Summit on Wednesday, September 3 rd
• Cantor Global Healthcare Conference 2025
  • Company presentation - Thursday, September 4 th starting at 3:20 p.m. ET
• Morgan Stanley 23 nd Annual Global Healthcare Conference
  • Company presentation - Monday, September 8 th starting at 8:30 a.m. ET
• Baird 2025 Global Healthcare Conference on Tuesday, September 9 th
• H.C. Wainwright 27 th Annual Global Investment Conference
  • Company presentation - Wednesday, September 10 th starting at 10:00 a.m. ET

Visit the Investors and Media section of Mirum’s corporate website for webcast links and additional information.

About Mirum Pharmaceuticals, Inc.

Mirum Pharmaceuticals, Inc. is a biopharmaceutical company dedicated to transforming the treatment of rare diseases affecting children and adults. Mirum has three approved medications: LIVMARLI® (maralixibat) oral solution/LIVMARLI® (maralixibat) tablets, CHOLBAM® (cholic acid) capsules, and CTEXLI™ (chenodiol) tablets.

LIVMARLI, an IBAT inhibitor, is approved for the treatment of two rare liver diseases affecting children and adults. It is approved for the treatment of cholestatic pruritus in patients with Alagille syndrome in the U.S. (three months and older), in Europe (two months and older), and in other regions globally. It is also approved in the U.S. in cholestatic pruritus in PFIC patients 12 months of age and older; in Europe, it is approved for patients with PFIC three months of age and older. Mirum is conducting the Phase 3 EXPAND study, a label expansion opportunity for LIVMARLI in additional settings of cholestatic pruritus. CHOLBAM is FDA-approved for the treatment of bile acid synthesis disorders due to single enzyme deficiencies and adjunctive treatment of peroxisomal disorders in patients who show signs or symptoms of liver disease.

CTEXLI is FDA-approved for the treatment of cerebrotendinous xanthomatosis (CTX) in adults.

Mirum's late-stage pipeline includes two investigational treatments for several rare diseases.

Volixibat, an IBAT inhibitor, is being evaluated in two potentially registrational studies including the Phase 2 VISTAS study for primary sclerosing cholangitis (PSC) and Phase 2b VANTAGE study for primary biliary cholangitis. Volixibat has been granted Breakthrough Therapy Designation for the treatment of cholestatic pruritus in patients with PBC. Mirum is also planning for a Phase 2 study evaluating MRM-3379, a PDE4D inhibitor for the treatment of Fragile X syndrome, a rare genetic neurocognitive disorder.

To learn more about Mirum, visit mirumpharma.com and follow Mirum on Facebook, LinkedIn, Instagram and X.

View source version on businesswire.com:https://www.businesswire.com/news/home/20250827209333/en/

CONTACT: Investor Contacts:

Andrew McKibben

[email protected] Contact:

Bryan Blatstein

Spectrum Science Communications

[email protected]

KEYWORD: UNITED STATES NORTH AMERICA CALIFORNIA

INDUSTRY KEYWORD: BIOTECHNOLOGY PHARMACEUTICAL HEALTH

SOURCE: Mirum Pharmaceuticals, Inc.

Copyright Business Wire 2025.

PUB: 08/27/2025 04:02 PM/DISC: 08/27/2025 04:02 PM

http://www.businesswire.com/news/home/20250827209333/en